Our peer-reviewed research publications represent the vanguard of genetic science. Discover breakthroughs and innovations driving the future of gene therapy.
Explore Key PapersLandmark study demonstrating 98% correction efficiency using our novel CRISPR-Sa9X delivery system for CFTR gene repairs.
Phase II clinical results showing 90% improvement in hemoglobin levels with no long-term side effects observed.
Published in Journal of Gene Medicine Aug 2024
Cell Reports, April 2024
Science, Jun 2024
All our peer-reviewed publications are freely accessible through our online database. Find detailed research protocols, clinical trial data, and full scientific reports.
Search PublicationsCollaborating with leading universities and research institutions worldwide to advance gene therapy science.
Partnering with biotech firms and pharmaceutical companies to develop innovative therapies and delivery methods.
Working closely with FDA, EMA and global regulatory bodies to establish standards for safe and effective gene therapies.